A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
CRIM-negative infantile Pompe disease: characterization of immune responses in patients treated with ERT monotherapy | Genetics in Medicine
PDF) CRIM-negative infantile Pompe disease: 42-Month treatment outcome
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Frontiers | A Race Against Time—Changing the Natural History of CRIM Negative Infantile Pompe Disease
Algorithm for the Early Diagnosis and Treatment of Patients with Cross Reactive Immunologic Material- Negative Classic Infantile
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Kaplan-Meler survival analysis: overall and invasive ventilator-free... | Download Scientific Diagram
Representative Western gel blot showing CRIM negative s | Open-i
CRIM status in PCMCs and fibroblasts, and GAA mutations, in 6 patients... | Download Table
Children | Free Full-Text | The Clinical Management of Pompe Disease: A Pediatric Perspective
The impact of antibodies on clinical outcomes in diseases treated with therapeutic protein: Lessons learned from infantile Pompe disease | Genetics in Medicine
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
Therapeutic Options for the Management of Pompe Disease: Current Chall | TCRM
Pompe Disease
Treatment approach for IOPD. CRIM, cross-reactive immunologic... | Download Scientific Diagram
Verification of CRIM status classification in patients with IOPD. | Download Table
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
JCI Insight - Sustained immune tolerance induction in enzyme replacement therapy–treated CRIM-negative patients with infantile Pompe disease
Pompe disease treatment: What are the options? | Pompe Disease News
Transforming the clinical outcome in CRIM-negative infantile Pompe disease identified via newborn screening: the benefits of early treatment with enzyme replacement therapy and immune tolerance induction | Genetics in Medicine
Child Neurology: Pompe disease | Neurology
IJNS | Free Full-Text | Newborn Screening for Pompe Disease: Pennsylvania Experience
A new assay for fast, reliable CRIM status determination in infantile-onset Pompe disease - ScienceDirect
Targeted approaches to induce immune tolerance for Pompe disease therapy: Molecular Therapy Methods & Clinical Development
